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Orchard Therapeutics
Orchard Therapeutics
(ORTX)
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Clinical Trials
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Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Atidarsagene autotemcel
metachromatic leukodystrophy
,
lysosomal storage diseases
Simoladagene autotemcel
severe combined immunodeficiency
Aspartame
myelodysplastic syndromes
,
aplastic anemia
Histone-arginine methyltransferase carm1
multiple myeloma
,
myeloid leukemia
,
hypercholesterolemia
,
atherosclerosis
,
plasma cell neoplasms
,
gastrointestinal neoplasms
,
intestinal neoplasms
,
nose neoplasms
,
b-cell lymphoma
,
hematologic neoplasms
,
non-hodgkin lymphoma
,
bcr-abl positive chronic myelogenous leukemia
,
hodgkin disease
,
obesity
,
alzheimer disease
,
myeloid leukemia acute
,
b-cell chronic lymphocytic leukemia
,
follicular lymphoma
,
large b-cell lymphoma diffuse
,
b-cell leukemia
,
hyperplasia
,
hepatocellular carcinoma
,
liver neoplasms
,
neoplasms
,
healthy volunteers/patients
,
depression
,
leukemia
,
small cell lung carcinoma
,
colorectal neoplasms
,
chronic hepatitis
,
arthritis
,
lymphoma
,
squamous cell carcinoma of head and neck
,
myeloid leukemia chronic-phase
,
bronchiolitis obliterans syndrome
,
hiv infections
,
hepatitis b virus
,
recurrence
,
ovarian neoplasms
,
fallopian tube neoplasms
,
clear cell adenocarcinoma
,
uveal neoplasms
,
cutaneous malignant melanoma
,
uveal melanoma
,
diabetic neuropathies
,
fibrosis
,
idiopathic pulmonary fibrosis
,
pulmonary fibrosis
,
hypertension
,
overweight
,
depressive disorder
,
neuralgia
,
postherpetic neuralgia
,
interstitial lung diseases
,
common variable immunodeficiency
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
pancreatic neoplasms
,
rectal neoplasms
,
urinary bladder neoplasms
,
head and neck neoplasms
,
squamous cell carcinoma
,
hepatitis c
,
hepacivirus
,
melanoma
,
prostatic neoplasms
,
non-small-cell lung carcinoma
,
breast neoplasms
,
chronic hepatitis c
,
diabetes mellitus
,
renal cell carcinoma
,
systemic lupus erythematosus
,
hiv
,
thrombosis
,
neoplasm metastasis
,
connective tissue diseases
,
immune system diseases
,
autoimmune diseases
,
venous thrombosis
,
pulmonary embolism
,
embolism
,
lung neoplasms
,
developmental disabilities
,
autism spectrum disorder
,
pervasive child development disorders
,
hepatitis
,
hepatitis a
,
type 2 diabetes mellitus
,
rheumatoid arthritis
,
hepatitis b
,
infections
,
chronic hepatitis b
,
atrial fibrillation
,
communicable diseases
,
lymphocytosis
,
systemic scleroderma
,
juvenile arthritis
,
psoriatic arthritis
,
ankylosing spondylitis
,
sjogren's syndrome
,
undifferentiated connective tissue diseases
,
joint diseases
,
sacroiliitis
,
mixed connective tissue disease
Surlorian
neoplasms
,
cancer pain
,
melanoma
,
oncogenes
,
thrombocytopenic purpura idiopathic
,
purpura
,
photosensitivity disorders
,
leukemia
,
lymphoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
multiple myeloma
,
plasma cell neoplasms
,
rheumatoid arthritis
,
cachexia
,
hepatitis c
,
chronic hepatitis c
,
chronic hepatitis b
,
hepatitis
,
chronic hepatitis
,
hepatitis a
,
overweight
,
anxiety disorders
,
social phobia
,
pruritus
,
covid-19
,
infections
,
hiv infections
,
acquired immunodeficiency syndrome
,
communicable diseases
,
rhinitis
,
immunologic deficiency syndromes
,
inflammatory breast neoplasms
,
atrial fibrillation
,
macular degeneration
,
tuberculosis
,
pulmonary tuberculosis
,
malaria
,
vivax malaria
,
thrombocytopenia
,
non-small-cell lung carcinoma
,
lung neoplasms
,
systemic lupus erythematosus
,
cough
,
common cold
,
dyslipidemias
,
diabetes mellitus
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
sclerosis
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
heart diseases
,
atherosclerosis
,
ovarian neoplasms
,
endometrial neoplasms
,
ovarian epithelial carcinoma
,
respiratory syncytial viruses
,
breast neoplasms
,
hypertension
,
postmenopausal osteoporosis
,
alzheimer disease
,
headache
,
personal satisfaction
,
hypersensitivity
,
dentin sensitivity
,
tension-type headache
,
inflammation
,
smoking
,
prostatic hyperplasia
,
dental caries
,
dysmenorrhea
,
mumps
,
measles
,
chickenpox
,
rubella
,
spinal cord injuries
,
erectile dysfunction
,
asthma
,
chronic obstructive pulmonary disease
,
lung diseases
,
migraine disorders
,
type 2 diabetes mellitus
,
acne vulgaris
,
prostatic neoplasms
,
back pain
,
hemorrhage
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